Targeted blockade of aberrant sodium current in a stem cellderived neuron model of SCN3A encephalopathy
Targeted blockade of aberrant sodium current in a stem cellderived neuron model of SCN3A encephalopathy
Guojie Qu, Julie P. Merchant, Jérôme Clatot, Leah M. DeFlitch, Danny J. Frederick, Sheng Tang, Madeleine Salvatore, Xiaohong Zhang, Jianping Li, Stewart A. Anderson, Ethan M. Goldberg